Scheie Syndrome - 32 Studies Found
Completed |
: A Study Investigating the Relationship Between the Development of Laronidase Antibody and Urinary GAG (Glycosaminoglycan) Levels in Aldurazyme® Treated Patients :
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Enrolling by invitation |
: Extension Study of AGT-181-102 to Evaluate Long Term Safety and Activity of AGT-181 : Mucopolysaccharidosis I : 2015-11-03 : Drug: AGT-181 intravenous infusion over 3-4 hours Ot |
Recruiting |
: Biomarker for Patients With Hurler Disease or High-grade Suspicion for Hurler Disease :
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Completed |
: A Study of Intrathecal Enzyme Therapy for Cognitive Decline in MPS I :
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Terminated |
: Extension Study of Intrathecal Enzyme Replacement Therapy for MPS I :
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Recruiting |
: Mucopolysaccharidosis I (MPS I) Registry : Mucopolysaccharidosis I (MPS I) : 2005-09-02 |
Active, not recruiting |
: Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic Disorders :
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Recruiting |
: Lysosomal Storage Disease: Health, Development, and Functional Outcome Surveillance in Preschool Children :
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